Kongress für Kinder- und Jugendmedizin 2019
zur Liste
Dr. med. Christian Werner
Frankfurt am Main Germany
  • Vortrag AGIL-AADC Gene Therapy Results in Sustained Improvements in Motor and Developmental Milestones over 5 Years in Children with AADC Deficiency Speaker
    Datum: 12.09.2019 , Zeit: 12:55 | Thema: GNP
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  • Vortrag Effect of ataluren on age at loss of ambulation in nonsense mutation Duchenne muscular dystrophy: observational data from the STRIDE Registry Speaker
    Datum: 12.09.2019 , Zeit: 12:15 | Thema: GNP
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  • Vortrag Ataluren in patients aged ≥ 2 to < 5 years with nonsense mutation Duchenne muscular dystrophy (nmDMD): 28-week results from a phase 2 study Speaker
    Datum: 12.09.2019 , Zeit: 12:20 | Thema: GNP
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