Vortrag
A Long-term, Prospective, Multicenter, In clinic and Online Disease Monitoring Program (DMP) for Patients with Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
Speaker
Vortrag
Clinical Outcomes of Major Clinical Events and Emergency Triheptanoin Use in Critically Ill Patients with Long-chain Fatty Acid Oxidation Disorders (LC-FAOD): A Retrospective Chart Review
Speaker